Mandy Reuschel
2 Papers
Mandy Reuschel is an academic researcher. The author has contributed to research in topics: Medicine. The author has an hindex of 2, co-authored 2 publications.
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Papers
Safety and efficacy of leriglitazone for preventing disease progression in men with adrenomyeloneuropathy (ADVANCE): a randomised, double-blind, multi-centre, placebo-controlled phase 2–3 trial
Wolfgang Köhler,Marc Engelen,Florian Eichler,Robin H. Lachmann,Ali Fatemi,Jacinda B. Sampson,Ettore Salsano,Josep Gamez,Márk Molnár,Sílvia Pascual,Maria Rovira,Anna Vilà,Guillem Pina,Itziar Martin-Ugarte,Adriana Mantilla,Pilar Pizcueta,Laura Rodríguez-Pascau,E. Traver,Anna Vilalta,María Rosa Querol Pascual,Marco Martiniello,U. Meya,Fanny Mochel,Eavan Mc Govern,Elise Yazbeck,Magali Barbier,Marie-Pierre Luton,Françoise Pousset,Jean-Yves Hogrel,Isaac M. Adanyeguh,Florian Then Bergh,Caroline G. Bergner,A. Unterlauft,Hannes Roicke,Karl-Titus Hoffmann,C. Scherlach,A. Al Kalb,Bianca Meilick,Mandy Reuschel,S Fenu,Elena Mauro,Elaine Murphy,G Sivarama Krishna,Tiggy Beyene,Alba Sierra,Sara Quiñoa,Anna Belen Canovas,Zoltán Grosz,Báthori Györgyi,S. I. V. D. Stadt,Irene C. Huffnagel,Wouter J.C. Van Ballegoij,M. Voermans,Reza Seyedsadjadi,Camille Corre,N. Godbole,Natalie Grant,Claudia Maria Brito Pires,M. K. Trovato,Nancy Yeh,J. Robyn Goodman,Jennifer Keller,Chris Joseph,Keith Van Haren,Sarada Sakamuri,Tina Duong,Lila A Perrone,Stephanie Tran,Sally Dunaway Young,S. Hashmi +69 more
TL;DR: The finding that cerebral adrenoleukodystrophy, a life-threatening event for patients with adrenomyeloneuropathy, occurred only in patients in the placebo group supports further investigation of whether leriglitazone might slow the progression of cerebral adrenoleskystrophy.
Safety and efficacy of rozanolixizumab in patients with generalised myasthenia gravis (MycarinG): a randomised, double-blind, placebo-controlled, adaptive phase 3 study
Vera Bril,Artur Druzdz,Julian Grosskreutz,Ali Habib,Renato Mantegazza,Sabrina Sacconi,Kimiaki Utsugisawa,John Vissing,Tuan Vu,Mary Boehnlein,Ali Bozorg,M. Gayfieva,Bernhard Greve,F. Woltering,Henry J. Kaminski,Angela Genge,Rami Massie,Maxime Bérubé,Lubna Daniyal,Shabber Mannan,Eduardo Ng,Ritesh Raman,Evelyn Sarpong,Monica Alcantara,Annie Dionne,Zaeem A. Siddiqi,Derrick Blackmore,Faraz S. Hussain,Genevieve Matte,Stephan A Botez,Michaela Tyblova,M. Jakubíkova,Jana Junkerova,Nanna Witting,Sonja Holm-Yildiz,Mads Godtfeldt Stemmerik,Henning Andersen,Izabella Obál,Guilhem Solé,Stéphane Mathis,Marie Helene Violleau,Christine Tranchant,Jean-Baptiste Chanson,Aleksandra Nadaj-Pakleza,Manuela Gambella,Michele Cavalli,Tanya Stojkovic,Sophie Demeret,Loïc Le Guennec,Giorgia Querin,N. Weiss,Marion Masingue,Laurent Magy,Karima Ghorab,I. Rukhadze,Alexander Tsiskaridze,M Janelidze,Temur Margania,Florian Then Bergh,A. Al Kalb,Bianca Meilick,Mandy Reuschel,A. Unterlauft,C. Goedel,Tim Hagenacker,Andreas Totzeck,Benjamin Stolte,Franz Blaes,Christine Bindler,Annekathrin Roediger,Christian Geis,Jens Schmidt,Jana Zschüntzsch,Stefanie Meyer,K. Kummer,Stefanie Glaubitz,Rachel Zeng,Heinz Wiendl,Luisa Klotz,Anna Lammerskitten,J. Lünemann,Péter Diószeghy,Lorenzo Maggi,Elena Rinaldi,Matteo Gastaldi,Federico Mazzacane,Pietro Businaro,Raffaele Iorio,Giovanni Antonini,Laura Fionda,Rita Rinaldi,Simone Rossi,Francesco Habetswallner,Francesco Tuccillo,Eiko Uenaka,Masanori Takahashi,Keiko Higashi,Makoto Kinoshita,Emi Yoneda,Noriko Nakamura,Tomoya Kubota,Masami Ono,Taku Hatano,Kazumasa Yokoyama,Yutaka Oji,Yuji Tomizawa,Akiyuki Uzawa,Manato Yasuda,Sachiko Akita,Yukiko Ozawa,Yosuke Onishi,Mikio Takaki,Hiromi Yamada,Kanako Minemoto,Nana Izawa,M. Nakayama,Masayuki Masuda,Nobuhiro Ido,Yoshihiko Okubo,Makiko Naito,Seiko Yoshida,Yuri Fukushige,Akira Tsujino,Atsushi Nagaoka,Teiichiro Miyazaki,Shunsuke Yoshimura,Takuro Hirayama,Tomoaki Shima,Naoko Okamoto,Rikizo Matsumoto,Kenji Sekiguchi,Takehiro Ueda,Norio Chihara,Emi Sunagawa,Ayaka Suzuki,Shigeaki Suzuki,Kei Ishizuchi,Yasushi Suzuki,Mitsuo Yata,Yuka Komatsu,Kenichi Tsukita,Genya Watanabe,Kazuki Saito,Emiko Kawasaki,Naoki Yamamoto,Hirohiko Ono,Tomoko Tsuda,Shigeki Ohashi,Yuka Fujisawa,Yumiko Yokota,Yuriko Nagane,Yuka Takematsu,Hiroyuki Naito,Konrad Rejdak,Sebastian Szklener,Tomasz Berkowicz,Paulina Budzińska,Marek Halas,Leonid Zaslavskiy,E. A. Skornyakova,Sergey Kotov,E. Novikova,Olga V. Churakova (Sidorova),V.V. Goldobin,Tatiana Alekseeva,P.S. Isabekova,Nadezhda Malkova,Denis Korobko,Gordana Djordjevic,Aleksandar Stojanov,Stojan Peric,Dragana Lavrnic,Ivo Bozovic,Aleksa Palibrk,Carlos Casasnovas,Velina Nedkova-Hristova,N. Fernández,Elena Cortes Vicente,Luis Antonio Querol Gutierrez,Maria Salvado Figueras,Raul Juntas Morales,Daniel Tejerina,Albert Saiz,Yolanda Morgado,Gerardo Gutiérrez Gutiérrez,Paqui Iniesta,J.E. Meca Lallana,Yuh-Cherng Guo,Hou Chang Chiu,Jiann-Horng Yeh,Ya Hui Chen,Mei Fen Lee,Yi-Chung Lee,Kuan Lin Lai,Said R. Beydoun,Salma Akhter,Lucy Lam,Alisha Thomas,Michael H. Rivner,Brandy Quarles,Dale L. Lange,Shara Holzberg,Pantelis Pavlakis,Radwa Aly,Lisa Ashworth,Kathryn E. Bender,K. Bond,Sara J. Byerly,James B. Caress,Catherine Franklin,M.P. Hiatt,Rachana Mehta,Gina Miller,Lynn Smith,Rose Ann Smith,Tahseen Mozaffar,I. Hernandez,K. S. Moulton,Chafic Karam,Pranali Ravikumar,Catherine Lomen-Hoerth,La Vergne Rosow,Hannah C George,Viktoriya S. Irodenko,Carol Denny,Sara Klein,Jennifer M. Martinez-Thompson,Elie Naddaf,Denny J. Padgett,Eric M. Sorenson,Kourosh Rezania,Jason R. Thonhoff,Sheetal Shroff,Robert M. Pascuzzi,Angela Micheels,Cynthia Bodkin,Adam Comer,Renee Wagner,Zabeen Mahuwala,Stephen A. Ryan,Kai-Hua Su,Khema R. Sharma,Andrew W. Brown,K.L. Liow +243 more
TL;DR: Reductions in MG-ADL score from baseline to day 43 were greater in the rozanolixizumab 7 mg/kg group than with placebo, and the primary efficacy endpoint was change from baseline-to-day 43 inMG- ADL score, assessed in the intention- to-treat population.