Simian retrovirus vectors for gene transfer in nonhuman primate cells.

Over 70 human diseases have been named as potential beneficiaries of somatic cell gene therapy, ranging from inherited disorders, such as cystic fibrosis and forms of severe combined immune deficiency, to cancer and AIDS (Scarpa and Caskey, 1989) Intervention by ‘designer genes’ incorporated into patients’ own cells could replace absent or defective molecules, synthesize metabolic enzymes or drugs, or manipulate the body’s immune responses (Ledley, 1990; Miller, 1990a) The realisation that recombinant DNA technology, now familiar in a diagnostic context, can be applied to the correction of diagnosed diseases is leading to a renewed optimism in the clinic for treating conditions that have so far persistently defeated more conventional therapeutic strategies

Retroviral-Mediated Gene Transfer and Duchenne Muscular Dystrophy

With the application of recombinant DNA technology to medical practice, geneticists have gained powerful tools for the diagnosis and therapy of genetic disease at the molecular level.

The Use of Retroviral Vectors in Human Disorders

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The Use of Retroviral Vectors in Human Disorders